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Orphan_Drug_Designation_List_governs_April-Jun 2014.xlsx
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Document Date: 2014-03-27 18:07:19


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City

Bristol / /

Company

Onconova Therapeutics Inc. / TESARO Inc. / Biopharmaceuticals Inc. / AbbVie Inc. / Designation Date Designation Contact Company / Contact Company/Sponsor Microbiotix Inc. / QLT Inc. / Lumena Pharmaceuticals Inc. / Atterocor Inc. / Ferrokin BioSciences Inc. / 273 Onconova Therapeutics Inc. / Zalicus Pharmaceuticals Ltd. / Catalyst Pharmaceutical Partners / Cyclacel Limited / Name Designation Date Designation Contact Company / CytRx Corporation / Mundipharma Research Limited / Murigenetics SAS Meritage Pharma Inc. / GlycoMimetics Inc. / Contact Company/Sponsor NATCO Pharma Limited Global / 273 Mundipharma Research Limited / 273 Eisai Inc. / Fujisawa / NephRx Corporation / ViroDefense Inc. / Novartis Pharmaceuticals / Pharmaceuticals' Inc. / Name Trade Name Designation Date Designation Contact Company / Trade Name Designation Date Designation Contact Company / AS NephRx Corporation / Otsuka Pharmaceutical Company Ltd / A2 Pharma / Astex Therapeutics Ltd / Teva / Generic Name Trade Name Contact Company / Research Ltd. / Infinity Pharmaceuticals Inc. / transplantation Inc. / Albireo AB / Auris Medical Inc. / NATCO Pharma Limited / Phase 2 Discovery Inc. / Fragile X syndrome Corp. / 273 AbbVie Inc / DARA BioSciences Inc. / Discoveries Inc. / 273 Convergence Pharmaceuticals Ltd. / /

Facility

University Medical / terminal UkUnhibitor / /

IndustryTerm

Treatment of pancreatic cancer / Treatment of Fragile X syndrome / Treatment of ovarian cancer / 4/2012 syndrome Prevention / cancer Treatment / Treatment of alagille syndrome / Treatment of chronic lymphocytic leukemia / Treatment of circadian rhythm sleep disorders / Treatment of Fabry's disease / /

MedicalCondition

TB / chronic lymphocytic leukemia / congential amaurosis / Glioma / cirrhosis / carcinoma / infantile spasms / related leukemias / peripheral neuropathy / leukemia AbbVie / pancreatic cancer TESARO / tumor / chronic iron / nonā€small cell lung Orphan Synergy cancer / cytomegalovirus infections / Radiation Syndrome / cell leukemia / cancer / schizophrenia / tumors / disease / eosinophilic esophagitis / poliovirus infection / Fabry's disease / neuralgia / myelogenous leukemia / prolymphocytic leukemia / Tooth disease / circadian rhythm sleep disorders / thrombocytopenic purpura / retinitis / tardive dyskinesia / tuberculosis / /

MedicalTreatment

chemotherapy / radiation / renal transplant / /

OperatingSystem

OSE / /

Organization

Center Foundation / Company/Sponsor NATCO Pharma Limited Global Alliance for TB Drug Development Pfizer Global Research and Development Treatment / /

/

Product

fluorouracil / nitro / /

Technology

radiation / API / chemotherapy / Drug Development / /

SocialTag