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Gene delivery / Molecular biology / Lipid storage disorders / Rare diseases / Medical research / Retina / Canavan disease / Neuronal ceroid lipofuscinosis / Vector / Biology / Health / Medicine


AAV Vectors for Gene Transfer NIH Office of Biotechnology Activities Sept 17, 2007
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Document Date: 2013-12-10 13:59:40


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Epilepsy / Hemophilia B / infantile neuronal ceroid lipofuscinosis / deficiency / Single Gene Disorders / Retinal disease / Canavan Disease / AAV Trials/Disease Target Target disease / /

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NIH office of Biotechnology Activities / Gene Transfer Safety Assessment Board / /

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Biotechnology / 1 Protocols / /

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