![Gene delivery / Molecular biology / Lipid storage disorders / Rare diseases / Medical research / Retina / Canavan disease / Neuronal ceroid lipofuscinosis / Vector / Biology / Health / Medicine Gene delivery / Molecular biology / Lipid storage disorders / Rare diseases / Medical research / Retina / Canavan disease / Neuronal ceroid lipofuscinosis / Vector / Biology / Health / Medicine](https://www.pdfsearch.io/img/a7691a5275dbd443676962f46be0fc17.jpg)
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MedicalCondition Epilepsy / Hemophilia B / infantile neuronal ceroid lipofuscinosis / deficiency / Single Gene Disorders / Retinal disease / Canavan Disease / AAV Trials/Disease Target Target disease / / Organization NIH office of Biotechnology Activities / Gene Transfer Safety Assessment Board / / Technology Biotechnology / 1 Protocols / /
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