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National Institutes of Health / Lipid storage disorders / Rare diseases / Bethesda /  Maryland / Tay–Sachs disease / Biomarker / Clinical trial / Grant / Medicine / Health / Nursing research


Executive Summary (1 page) including major objectives and impact of
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Document Date: 2014-12-08 16:18:58


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City

Boston / /

Company

Sachs & Allied Diseases Association Inc. / /

Currency

USD / /

/

Facility

Beacon Street / /

/

IndustryTerm

clinical research networks / pre-applications / /

MedicalCondition

rare diseases / Diseases / disease / lysosomal storage diseases / genetic diseases / neurodegenerative disorders / especially lysosomal storage disorders / /

MedicalTreatment

gene therapy / /

Organization

Research Evaluation Subcommittee / National Institute of Health / Corporate Advisory Council / NTSAD’s Scientific Advisory Committee / /

Person

Grant Policies / Sue Kahn / /

/

Position

investigator / Principal Investigator / Executive Director / Director / NTSAD Phone / /

ProvinceOrState

Massachusetts / /

Technology

gene therapy / drug delivery / drug discovery / stem cells / drug screening / /

URL

www.ntsad.org / /

SocialTag