![Genetics / Biology / Spliceosome / Gene expression / RNA splicing / DNA / Genetic engineering / Exon / CEP290 / CRISPR / Cas9 / Guide RNA Genetics / Biology / Spliceosome / Gene expression / RNA splicing / DNA / Genetic engineering / Exon / CEP290 / CRISPR / Cas9 / Guide RNA](https://www.pdfsearch.io/img/2ac07a59520864cc34817388bde5cd4f.jpg) Date: 2016-08-22 09:22:03Genetics Biology Spliceosome Gene expression RNA splicing DNA Genetic engineering Exon CEP290 CRISPR Cas9 Guide RNA | | Therapeutic Correction of an LCA-Causing Splice Defect in the CEP290 Gene by CRISPR/Cas-Mediated Genome Editing Morgan L. Maeder, Rina Mepani, Sebastian W. Gloskowski, Maxwell N. Skor, McKensie A. Collins, Gregory M. GotAdd to Reading ListSource URL: www.editasmedicine.comDownload Document from Source Website File Size: 492,51 KBShare Document on Facebook
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