| Document Date: 2011-12-11 11:39:13 Open Document File Size: 35,91 KBShare Result on Facebook
Company Amicus Therapeutics / / Country United States / / / Event FDA Phase / / IndustryTerm treatment of Fabry disease / biopharmaceutical / therapies for rare diseases / candidate drug products / therapy for Pompe disease / / MedicalCondition rare diseases / disease / lysosomal storage disorders / Fabry disease / diseases / lysosomal storage diseases / lysosomal storage disease / respiratory insufficiency / deficiency / Pompe disease / progressive skeletal muscle weakness / / MedicalTreatment Enzyme Replacement Therapy / / Person John F. Crowley / Pol F. Boudes / / / Position Chief Medical Officer / Chairman and Chief Executive Officer / Private / / Product in / Amigalâ„¢ (migalastat HCl) / AT2220 / / Technology alpha / / URL www.pompestudy.com / www.clinicaltrials.gov / /
SocialTag |