H. Kallwass S.P. / StataCorp LP College / P.E. Rao S.P. / Y.T. Chen D.D. / J.H. Kamphoven L.P. / Ó 2009 Elsevier Inc. / ARTICLE IN PRESS / IgG / Grant / A. Bird S.P. / Genzyme Corporation / D. Lillicrap S.A. / Y. An S.P. / Synpac Inc. / Y.H. Messinger A.S. / /
Continent
Europe / /
Country
Netherlands / Canada / Israel / Taiwan / United States / /
Currency
pence / / /
Event
FDA Phase / /
Facility
Duke Clinical Research Institute / Science University / Institute of Biomedical Sciences / Duke University / College Station / Rambam Medical Center / Duke University Medical Center / / /
IndustryTerm
treatment of Pompe disease / therapy for infantile Pompe disease / therapy for Fabry disease / therapy for Pompe disease / tolerance-inducing protocols / newborn screening protocols / therapies for other lysosomal storage disorders / therapy for infantile glycogen storage disease / therapy for Gaucher disease / /
MarketIndex
LVM / /
MedicalCondition
hypertrophic cardiomyopathy / lysosomal storage disorders / treatable disease / anaphylaxis / canine mucopolysaccharidosis I / storage disorder / immune complex-mediated nephritis / cardiomyopathy / hemophilia A / respiratory failure / infantile glycogen storage disease / Gaucher disease / Fabry disease / motor disease / severe hemophilia A / rapidly progressive muscle weakness / Haemophilia / glycogen storage disease / reverse cardiomyopathy / MS / severe thrombotic thrombocytopenic purpura / disease / hemophilia B / nephrotic syndrome / mucopolysaccharidosis I / each disease / /
Division of Speech / Neonatology / Oregon Health and Science University / Portland / United States Food and Drug Administration / Science University / Portland / Division of Medical Genetics / Pompe / European Union / Rambam Medical Center / Division of Therapeutic Proteins / Department of Pediatrics / Division of Neonatology / Duke University / Durham / USA Department of Surgery / Pompe and Gaucher Registry Boards / Pediatrics / Medicine / and Duke Clinical Research Institute / Institute of Biomedical Sciences / Division of Speech and Hearing / US Food and Drug Administration / National Center for Research Resources / and the National Institutes of Health / Center for Drug Evaluation and Research / Duke University Medical Center / /
Person
Priya S. Kishnani / J. Clin / Sue Ann Smith / L. Klinge / V / P. Van Diggelen / Katherine Lewis / Stephanie L. DeArmey / Deya Corzo / H. Waldmann / M. Van den Hout / Sarah Young / Amy Rosenberg / Skip lane / James Heller / J. Van Corven / Paula C. Goldenberg / A. Schulz / V / Susan Richards / Hanna Mandel / J.A. Smeitink / Jennifer S. Li / Alberta Infant / H. Van Hirtum / H.H. Kazazian Jr. / L. Van Hove / D.S. Millar / V / Danny Benjamin / A. Van Doorn / H. Van den Hout / J. Van Hove / C. Tanaka / V / B. de Klerk / J. Pediatr / /
Position
disease model / physical therapist / Major / Representative / Advisors / Corresponding author / Fisher / member / G.P. / D.J. / /
Microsoft Word - fig1_FINAL.doc