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Rare diseases / Glycogen storage disease type II / Hepatology / Lysosomal storage disease / Acid alpha-glucosidase / Salbutamol / Enzyme replacement therapy / Methadone / Medicine / Chemistry / Health


The FASEB Journal • Research Communication Adjunctive albuterol enhances the response to enzyme replacement therapy in late-onset Pompe disease Dwight D. Koeberl,*,1 Stephanie Austin,* Laura E. Case,† Edward C. Smit
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Document Date: 2014-08-13 23:54:32

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City

Porto / KOEBERL ET / Chen / Bercury / La Jolla / Cambridge / Durham / Florence / /

Company

Koeberl D. D. / AEs / Zivkovic S. A. / McDermott / Young S. P. / Beek N. A. / Genzyme Corp. / Koeberl D. D. Li / /

Country

United States / /

Currency

USD / /

/

Event

FDA Phase / /

Facility

Scale bar / Duke University Medical Center / /

IndustryTerm

electronic paging device / Telephone visits / ADJUNCTIVE ALBUTEROL IN POMPE DISEASE therapy / treatment of Pompe disease / /

MedicalCondition

neuromuscular disorders / muscular dystrophy / late-onset Pompe disease Dwight D. Koeberl / chronic heart disease / significant pulmonary compromise / GAA deficiency / lysosomal storage disorders / late-onset Pompe’s disease / IN POMPE DISEASE / hyperthyroidism / tremor / glycogen storage disease / hypersensitivity / pulmonary function testing / infantile-onset Pompe disease / Pompe disease / ADJUNCTIVE ALBUTEROL IN POMPE DISEASE / late-onset Pompe disease / pulmonary function tests / seizure disorder / facioscapulohumerol muscular dystrophy / murine Pompe disease / acid maltase deficiency / muscle disorder glycogen storage disease / mild urinary retention / interstitial stroma/ fibrosis / fibrosis / /

MedicalTreatment

enzyme replacement therapy / /

Organization

Department of Pathology / Division of Pediatric Genetics / Department of Pediatrics / Duke University Institutional Review Board / Division of Physical Therapy / Division of Medical Genetics / Duke University Medical Center / /

Person

Gene Tex / Jian Dai / Priya S. Kishnani / Lange / Sarah P. Young / Park / Dwight D. Koeberl / Leshner / Carla Johnson / Pestronk / Songtao Li / /

Position

D. J. / King / pathologist / Representative / /

Product

albuterol / ERT / /

ProvinceOrState

Bali / Alabama / South Dakota / North Carolina / Y. T. / /

PublishedMedium

The FASEB Journal / /

Technology

alpha / paging / Flash / encoding human acid-alpha-glucosidase / /

URL

www.fasebj.org / /

SocialTag