Back to Results
First PageMeta Content
Organ failure / Pain / Kidney diseases / Clinical research / Fabry disease / Neuropathic pain / Chronic kidney disease / Placebo / Renal failure / Medicine / Health / Biology


ORIGINAL CONTRIBUTION Enzyme Replacement Therapy in Fabry Disease A Randomized Controlled Trial Raphael Schiffmann, MD
Add to Reading List

Document Date: 2014-10-06 21:28:23

Open Document

File Size: 221,39 KB

Share Result on Facebook

City

Houston / New York / Washington / DC / Cambridge / /

Company

Balk AG / Clague AE / IgG / Transkaryotic Therapies Inc / Blieden LC / Cox / Becker AE / Gal AE / Sirvent AE / /

Country

France / Singapore / /

/

Event

Product Recall / FDA Phase / Product Issues / /

Facility

M. D. Anderson Cancer Center / National Institute of Diabetes / National Institute of Neurological Disorders / Armed Forces Institute of Pathology / Rockville Pike / Clinical Research Center / /

IndustryTerm

treatment of Gaucher’s disease / treatment of patients with Fabry disease / organ systems / placebo / therapy for Fabry disease / /

MedicalCondition

DF / chronic neuropathic pain medication regimens / lysosomal storage disorders / oligoanuric end-stage renal failure / cerebrovascular disease / endstage renal disease / inherited enzyme deficiency / Fabry’s disease / Glomerular diseases / ENZYME REPLACEMENT THERAPY IN FABRY DISEASE / interstitial fibrosis / renal disease / right bundle-branch block / metabolic disorders / end-stage renal disease / illness / constipation / hearing loss / dorsal root ganglion / X-LINKED recessive glycosphingolipid storage disorder / proteinuria / abdominal pain / diabetic nephropathy / Early renal failure / MaroteauxLamy syndrome / cancer / neuropathic pain syndrome / disease / Progressive glomerular injury Context Fabry disease / Kidney Diseases / damaged dorsal root ganglion / Kahn P. Anderson-Fabry disease / interstitial inflammation / cardiovascular disease / episodic diseases / pain / Fabry disease / Inherited Disease / metastatic cancer / Gaucher’s disease / diseases / rigors / coronary artery disease / AIDS / deficiency / metabolic disease / metabolic disorder / renal failure / small-fiber peripheral neuropathy / debilitating neuropathic pain / /

MedicalTreatment

premedication / peritoneal dialysis / Intravenous infusions / intravenous infusion / ENZYME REPLACEMENT THERAPY / Kidney Transplant / Renal Dialysis / /

Organization

Repeated administration / National Institute of Diabetes / Forces Institute of Pathology / National Institute of Neurological Disorders and Stroke / Division of Nephropathology / Clinical Research Center of the National Institutes of Health / American Medical Association / /

Person

Controlled Trial Raphael Schiffmann / Raphael Schiffmann / Jeffrey B. Kopp / Ann Neurol / Thais Weibel / Habib R. Early / James E. Balow / Peter Daniel / Ellen Vaughan / Cheryl Hipple / Howard A. Austin / Connie Kreps / Ann Acad Med / Sharda Sabnis / Virginia Stryker / Ashwini Chavan / Roscoe O. Brady / David F. Moore / /

/

Position

pharmacist / Corresponding Author / Author / Bishop / representative / /

Product

sodium chloride / pain medication / carbamazepine / phenytoin / Randomized 14 Assigned / Personal / lamotrigine / gabapentin / Gb3 / /

ProvinceOrState

Massachusetts / /

Technology

antibodies / transplantation / Dialysis / /

URL

www.jama.com / /

SocialTag