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Factor VIII / Antithrombin III deficiency / Antithrombin / Thrombin / Fibrinogen / Factor VII / Factor X / Haemophilia / Aluminium nitride / Coagulation system / Blood / Biology


2014 ASH Annual Meeting Special Scientific Symposium on RNA Therapeutics in Hematology RNAi Therapeutics for Hemophilia and Complement-Related Diseases Akin Akinc, PhD
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Document Date: 2014-12-08 15:55:27


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File Size: 1,94 MB

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Company

Alnylam Pharmaceuticals / /

Country

United States / /

Currency

USD / /

Event

FDA Phase / /

Facility

Stable Thrombus / /

IndustryTerm

Therapeutics for Hemophilia / /

MedicalCondition

Antithrombin deficiency / C deficiency / complement-mediated diseases / FIX FVIII FX FVIIIa FVIIa FVII Hemophilia B / Hemophilia A / Virus Infection ALN-HBV Beta-Thalassemia/Iron-Overload Disorders ALN-TMP Mixed Hyperlipidemia/Hypertriglyceridemia ALN / factor Blood clot / rare bleeding disorders / Human AT deficiency / SAD / Haemophilia / Patisiran (ALN-TTR02) TTR-Mediated Amyloidosis ALN-TTRsc ALN-AT3 Hemophilia / Hemophilia B / Hemophilia / S deficiency / Injuries / /

Organization

European Union / /

Person

Brian Cooley Saline / Akin Akinc / Lacra Ivanciu / Rodney Camire / /

Position

HB / HA/HB / /

Product

TTR02 / Whinna1 / /

Technology

Alpha / Laser / siRNA / /

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