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Extrinsic extensor muscles of the hand / Sialic acid / Muscle / Anatomy / Carbohydrate chemistry / Hereditary inclusion body myopathy


A Phase I Compassionate Trial of Nanocomplex Mediated GNE Gene Replacement in Hereditary Inclusion Body Myopathy-2
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Document Date: 2014-01-06 12:30:15


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File Size: 324,85 KB

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MedicalCondition

fever / /

Organization

FDA / Intramuscular Administration / /

Product

Sialic Acid Dependent Proteins L-ERCL Muscle Biopsy Pre/Post GNE Lipoplex Injection / FN Minimi / IM injection / Left Extensor Compartment Muscles Since Left ECRL Injection / /

Technology

Recombinant DNA / CMP / /

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