“NIH” Protocol Direct CNS Administration of a Replication Deficient Adeno-associated Virus Gene Transfer Serotype rh.10 Expressing the Human CLN2 cDNA to Children with Late Infantile Neuronal - Infantile neuronal ceroid lipofuscinosis - Document - PDFSEARCH.IO

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	“NIH” Protocol Direct CNS Administration of a Replication Deficient Adeno-associated Virus Gene Transfer Serotype rh.10 Expressing the Human CLN2 cDNA to Children with Late Infantile Neuronal Add to Reading List Document Date: 2013-12-31 10:40:24 Open Document File Size: 1,43 MB Share Result on Facebook Facility R. Crystal Weill Cornell Medical College / / IndustryTerm administration site / / MedicalCondition Batten Disease / vegetative state / Late Infantile Neuronal Ceroid Lipofuscinoses / Cognitive impairment / Late Infantile Neuronal Ceroid Lipofuscinosis RAC / Disease / Late Infantile Neuronal Ceroid Lipofuscinosis / seizures / / MedicalTreatment surgery / / Organization Direct CNS Administration / R. Crystal Weill Cornell Medical College / National Institute of Health / Cornell / AAVrh.10hCLN2 CNS Administration on Behavior of Non-human Primates / AAVrh.10hCLN2 Administration / / PublishedMedium Primates / / Technology Gene Therapy / MRI / / SocialTag Neuronal ceroid lipofuscinosis Medicine Batten disease Adeno-associated virus Infantile neuronal ceroid lipofuscinosis NCL Lipofuscin Lipid storage disorders Rare diseases Health

“NIH” Protocol Direct CNS Administration of a Replication Deficient Adeno-associated Virus Gene Transfer Serotype rh.10 Expressing the Human CLN2 cDNA to Children with Late Infantile NeuronalAdd to Reading List