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NNPDF Grant #47 – Fran Platt TARGETING SPHINGOSINE STORAGE AS A NEW THERAPEUTIC APPROACH FOR NIEMANN-PICK TYPE C 6 month report Lay Summary We have discovered that NPC cells have dramatically lower lysosomal
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Document Date: 2010-04-26 15:39:53
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File Size: 24,32 KB
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MedicalCondition
NPC1 disease /
disease /
/
Person
Fran Platt /
/
SocialTag
Lipid storage disorders
Rare diseases
Lipids
Miglustat
Piperidines
NPC1
Curcumin
Sphingomyelin
Niemann–Pick disease
Biology