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Lipid storage disorders / Rare diseases / Lipids / Miglustat / Piperidines / NPC1 / Curcumin / Sphingomyelin / Niemann–Pick disease / Biology / Chemistry / Biochemistry


NNPDF Grant #47 – Fran Platt TARGETING SPHINGOSINE STORAGE AS A NEW THERAPEUTIC APPROACH FOR NIEMANN-PICK TYPE C 6 month report Lay Summary We have discovered that NPC cells have dramatically lower lysosomal
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Document Date: 2010-04-26 15:39:53


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NPC1 disease / disease / /

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Fran Platt / /

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