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Clinical pharmacology / Food and Drug Administration / Therapeutics / United States Public Health Service / Pharmaceutical sciences / Clinical research / Pharmacology


January 14, 2014 The Honorable Margaret Hamburg, Commissioner Food and Drug Administration[removed]New Hampshire Ave. Silver Spring, MD 20993
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Document Date: 2014-01-14 15:47:20


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City

Washington / DC / /

Company

BioMarin / /

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IndustryTerm

treatment for this rare disease / /

MedicalCondition

Rare Diseases / disease / rare disease / Mucopolysaccharidosis IVA / rare disorder / /

Organization

Congress / office of New Drugs / Food and Drug Administration / National Organization for Rare Disorders / 19th Advisory Committee / office of Orphan Product Development Page / Advisory Committee / Center for Drug Evaluation / /

Person

Anne Pariser / Gayatri Rao / Robert J. Smith / Deanna Cisneros / Joseph Crowley / /

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Position

Director for Rare Diseases / Director / President and CEO / registered nurse / Commissioner / acting chairperson / representative / Director Woodcock / /

ProgrammingLanguage

DC / /

ProvinceOrState

Maryland / /

Technology

drug development / /

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