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Rare diseases / Medicine / Niemann–Pick disease / Niemann-Pick disease /  type C / Cyclodextrin / Lysosomal storage disease / European Medicines Agency / Miglustat / Orphan drug / Health / Chemistry / Lipid storage disorders


Document Date: 2013-07-21 06:20:11


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City

London / /

Continent

Europe / /

Country

Norway / United States / Iceland / Liechtenstein / United Kingdom / /

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Facility

Canary Wharf / /

IndustryTerm

treatment of Niemann-Pick disease / treatment of NiemannPick disease / orphan medicinal products / /

MedicalCondition

rare diseases / disease / NiemannPick disease / Niemann Pick disease / Niemann-Pick disease / Niemann-Pick disease type C / inherited disorders / lysosomal storage diseases / metabolic disorders / /

Organization

European Medicines Agency / Committee for Orphan Medicinal Products Public / European Commission / European Union / European Organisation for Rare Diseases / E-mail info@ema.europa.eu Website www.ema.europa.eu An / Committee for Orphan Medicinal Products / /

Person

Susan French / Lane Beaconsfield Buckinghamshire / /

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Product

Zavesca / /

Technology

av / /

URL

www.ema.europa.eu / /

SocialTag