![Rare diseases / Science / Clinical research / Design of experiments / Biotechnology / Niemann–Pick disease / Clinical trial / Lysosomal storage disease / Biomarker / Health / Medicine / Lipid storage disorders Rare diseases / Science / Clinical research / Design of experiments / Biotechnology / Niemann–Pick disease / Clinical trial / Lysosomal storage disease / Biomarker / Health / Medicine / Lipid storage disorders](https://www.pdfsearch.io/img/63854e2ba870c805583c30b26e6cd776.jpg)
| Document Date: 2013-11-05 17:37:54 Open Document File Size: 332,59 KBShare Result on Facebook
City Copenhagen / / Continent Europe / / Country United States / / / Facility Oxford University / / IndustryTerm treatment of Niemann-Pick Disease / therapy for the treatment of diseases / clinical and imaging markers / / MedicalCondition Niemann-Pick Disease type C. rhHSP70 / sphingolipidoses / diseases / lysosomal functional deficiency / lysosomal storage disease / clinical and biological disease / natural disease / extremely rare disease / marked disease / Niemann-Pick Disease / / Organization FDA / European Union / Oxford University / MHRA / Danish Agency / Swedish Medicinal Products Agency / / Person Thomas Kirkegaard Jensen / Marja Jäättela / / / Position representative / Professor / / URL www.orphazyme.com / /
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