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Lipid storage disorders / Rare diseases / Niemann–Pick disease / Lactones / Statins / Cyclodextrin / NPC1 / Cerebrospinal fluid / Cholesterol / Medicine / Chemistry / Health


Document Date: 2010-09-07 18:10:47


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Gothenburg / Geneva / Neville / Specific Blood / Venice / Tokyo / Philadelphia / Stockhom / Prague / Reno / Oakland / Adelaid / /

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Italy / Sweden / South Africa / Japan / United States / Australia / Finland / /

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pence / /

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pharmacy SOP / Sahlgrenska University Hospital / Research Center / Kings College / University St. Louis / Children’s Hospital of Oakland / University of Texas Southwestern / Stanford University / Karolinska Institute / National Cancer Institute / Children’s Hospital / Mayo Clinic / Pediatric Hematology Oncology Children's Hospital / Albert Einstein College of Medicine / University of Alberta / Dr. Kaj Blennow University of Goteborg / Renown Regional Medical Center / University of Pennsylvania / /

IndustryTerm

experimental protocol / histopaque solution / therapy for this devastating neurologic disorder / cellular cholesterol processing / fish oil / complementation / amyloid processing enzymes / imaging / enclosed intrathecal protocol / aseptic processing / Chemical properties / ml solution / treatment of Niemann Pick Type C disease / predicted protein product / intrathecal protocol / preparation protocol / treatment protocol / oxidation product / /

Person

Sarah Ward / David Begley / Niklas Mattsson / Kaj Blennow / Cassidy Helene Hempel / Jung H. Suh / Cassidy Miglustat / Cassi Addi Cassi Addi Cassi / Ingemar Björkhem / Caroline Hastings / Addison Miglustat / Jean Vance / Charles C. Pontikis / Chris Hempel / Joan E. Blanchette-Mackie / Henrik Zetterberg / Hugh Hempel / Edward B. Neufeld / Marie T. Vanier / Jill A. Morris / Charles Vite / Kinuko Suzuki / Timothy Cote / D. Scherrer / Steven Walkley / Christine Hempel / Ruyi He / John Dietschy / Marc C. Patterson / Eugene Carstea / Daniel Ory / Addison Ruth Hempel / Jung Suh / /

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Methylprednisolone / SC / acetylcysteine / sufentanil / alfentanil / Zavesca / Albuterol / propofol / F-18 / Epinephrine / fentanyl / lovastatin / /

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Alberta / Maryland / Nevada / Oregon / Pennsylvania / Nova Scotia / Florida / California / Colorado / /

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Pediatric Research / /

Region

South Africa / southern Colorado / /

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Neuroscience / treatment protocol / hybridization / enclosed intrathecal protocol / HPBCD INTRATHECAL TREATMENT PROTOCOL / 12 PROPOSED HPBCD INTRATHECAL TREATMENT PROTOCOL / MRI / pharmacokinetics / HPBCD intrathecal protocol / 6 HPBCD Approved FDA Treatment Protocol / Buffer preparation protocol / chemotherapy / revised protocol / experimental protocol / CAT / /

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