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Medical statistics / NPC1 / Clinical research / Design of experiments / Clinical trial / Biomarker / Surrogate endpoint / Histone deacetylase inhibitor / Niemann-Pick disease /  type C / Medicine / Health / Epidemiology


New NP-C Drug Trial A clinical trial is expected to begin in the summer of 2014 using a Histone Deacetylase Inhibitors (HDACi). The goal of the Phase 1 clinical trial will be to establish the safety and tolerability of a
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Document Date: 2013-12-11 15:45:47


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City

Rochester / /

Facility

University of Notre Dame / Mayo Clinic / Washington University / College of Science / National Institutes of Health Clinical Center / Maxfield laboratory / Columbia University / /

IndustryTerm

treatment for NPC1 disease / treatment of this devastating disorder / /

MedicalCondition

ataxia / dysarthria / dementia / disease / seizures / dysphagia / neurological manifestation / disorder / NPC1 disease / dystonia / vertical supranuclear gaze palsy / /

Organization

Columbia University / National Institute of Health / Food and Drug Administration / National Institutes of Health Clinical Center / College of Science / Cornell / NIH Clinical Center / FDA / Washington University / University of Notre Dame / /

Person

Olaf Wiest / Paul Helquist / Fred Maxfield / Porter / Steven Sturley / Marc Patterson / Ory / Greg Crawford / /

Position

Porter / Dean / /

ProvinceOrState

Minnesota / /

SocialTag