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Date: 2015-04-01 10:25:49Fabry disease Lysosomal storage disease Medicine Fabry Genetic disorder Lipid storage disorders Rare diseases Health | Fabry AwarenessPDF1Add to Reading ListSource URL: www.shire.comDownload Document from Source WebsiteFile Size: 971,75 KBShare Document on Facebook |
How one patient with a rare disease coped with his genetic disorderDocID: 1r9mW - View Document | |
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What is HUNTER SYNDROME? Hunter syndrome, or mucopolysaccharidosis II (MPS II), is a rare and progressive lysosomal storage disease inherited in an X-linked recessiveDocID: 1lIxr - View Document | |
MUCOPOLYSACCHARIDOSES Rare Diseases Unit of the Finnish Association of People with Physical Disabilities Support for this guide was provided by Genzyme.DocID: 1fJSQ - View Document | |
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