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Pharmacology / Research / Bioethics / Medical ethics / Genetic engineering / Ataluren / Duchenne muscular dystrophy / Placebo / Medicine / Clinical research / Science


Phase 3 Study of Ataluren in Patients with Nonsense Mutation Duchenne Muscular Dystrophy: Frequently Asked Questions What is ataluren? Ataluren (formerly called PTC124®) is an investigational new drug, which means it is
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Document Date: 2013-11-30 21:08:11


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