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Mutagenesis / Viral vector / CDKN2A / ABCD1 / Biology / Genetics / Insertional mutagenesis


Retroviral and Lentiviral Vectors for Long-Term Gene Correction: Clinical Challenges in Vector and Trial Design December 9, 2010, Bethesda Mouse Models for Predicting Insertional Mutagenesis
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Document Date: 2014-01-08 12:16:33


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Cdkn2a deficient SA / Totals Sample LC / /

Event

Product Issues / /

Facility

Predicting Insertional Mutagenesis Eugenio Montini San Raffaele Telethon Institute / /

MedicalCondition

Adrenoleukodystrophy / /

MedicalTreatment

gene therapy / /

Organization

Predicting Insertional Mutagenesis Eugenio Montini San Raffaele Telethon Institute for Gene Therapy HSR-TIGET Milan / /

Person

Alessandra Biffi / /

Product

SA-80 / /

Technology

Gene Therapy / /

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