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Company European Reference Networks / Directorate-General / / Continent Europe / / Country France / Slovakia / United Kingdom / / Currency EUR / / IndustryTerm treatment for patients suffering from a rare disease / treatment of rare diseases / associations producing products / therapies for rare diseases / treatment for the rare genetic disorder / online source / specialised healthcare / care for patients with inherited bleeding disorders / healthcare / pharmaceutical / expert / medicinal products / treatment for their disease / orphan medicinal products / / MedicalCondition allergies / rare diseases / cancer / _Communication_on_Rare_Diseases / disease / rare cancers / low prevalence complex diseases / single disease / dystrophic epidermolysis bullosa / rare diabetes / rare disease / rare / heritable disorders / _International_Rare_Diseases_Research_Consortium_ / inherited bleeding disorders / skin disease / international research effort Rare diseases / rare disorders / European haemophilia / diseases / disorder / such diseases / biggest collective rare diseases / autoinflammatory diseases / infections / different rare diseases / disorders / Black Bone Disease / / MedicalTreatment gene therapy / / Organization European Commission / European Union / European Organisation for Rare Diseases / Joint Research Centre / / Person Marina Cavazzana-Calvo / / Technology gene therapy / an information network / / URL http /
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