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Muscular dystrophy / Biotechnology / Duchenne muscular dystrophy / Sarepta Therapeutics / PTC Therapeutics / Exon skipping / Clinical trial / BioMarin Pharmaceutical / Draft:BMN 044 / Draft:SRP-4044
Date: 2016-01-26 12:45:27
Muscular dystrophy
Biotechnology
Duchenne muscular dystrophy
Sarepta Therapeutics
PTC Therapeutics
Exon skipping
Clinical trial
BioMarin Pharmaceutical
Draft:BMN 044
Draft:SRP-4044

ROUNDTABLE SURVEY RESULTS Our pilot program in 2015 was very successful. We distributed and collected surveys from all 6 of our Roundtable events, which were held in Boston, MA, Pittsburgh, PA. Los Angeles, CA and Dubl

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