Gene Transfer Clinical Trial for Spinal Muscular Atrophy Type 1 This study is a phase I, single-site, dose escalation study to evaluate the safety and efficacy of gene transfer for Spinal Muscular Atrophy Type 1 (SMA1). - Spinal muscular atrophy - Document - PDFSEARCH.IO

First Page	Meta Content
	Gene Transfer Clinical Trial for Spinal Muscular Atrophy Type 1 This study is a phase I, single-site, dose escalation study to evaluate the safety and efficacy of gene transfer for Spinal Muscular Atrophy Type 1 (SMA1). Add to Reading List Document Date: 2014-05-01 04:18:01 Open Document File Size: 266,99 KB Share Result on Facebook / Facility Gene Therapy The Research Institute / Nationwide Children’s Hospital / / MedicalCondition diabetes mellitus / HIV / disease / myopathy / Active viral infection / hepatitis B / / MedicalTreatment Gene Therapy / immunosuppressive therapy / / Organization Research Institute / Nationwide Children’s Hospital in Columbus / Sohyun McElroy Center / / / Position physician / researcher / care physician / study coordinator / / Product cyclosporine / cyclophosphamide / / ProvinceOrState Ohio / / Technology Gene Therapy / / SocialTag Biology SMN1 Gene therapy Clinical trial Invasiveness of surgical procedures Spinal muscular atrophies Medicine Health Motor neurone disease

Gene Transfer Clinical Trial for Spinal Muscular Atrophy Type 1 This study is a phase I, single-site, dose escalation study to evaluate the safety and efficacy of gene transfer for Spinal Muscular Atrophy Type 1 (SMA1).Add to Reading List