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Motor neurone disease / Spinal muscular atrophy


Dear Spinal Muscular Atrophy Community Members, We would like to update you on the clinical development of RG7800, an investigational SMN2 splicing modifier that is being studied as a potential treatment for spinal muscu
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Document Date: 2015-05-07 03:16:04


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Company

Rare Diseases F. Hoffmann-La Roche Ltd / /

IndustryTerm

study protocol / /

MedicalCondition

spinal muscular atrophy / /

Organization

SMA Foundation / /

Person

Luca Santarelli / Stuart Peltz / /

Position

CEO PTC Therapeutics Loren Eng President / VP / Head / /

Technology

Neuroscience / study protocol / pharmacokinetics / /

SocialTag