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Pancreas disorders / Anilides / Ivacaftor / Phenols / Quinolones / Cystic fibrosis transmembrane conductance regulator / Cystic fibrosis / Congenital absence of the vas deferens / Vertex Pharmaceuticals / Biology / Health / Medicine


CI-1 KALYDECO® (Ivacaftor) Treatment for Cystic Fibrosis Vertex Pharmaceuticals Incorporated Pulmonary and Allergy Drugs
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Company

CF / Clinical Development Vertex Pharmaceuticals Incorporated / Global Regulatory Affairs Vertex Pharmaceuticals Incorporated / Cystic Fibrosis Vertex Pharmaceuticals Incorporated / /

Event

FDA Phase / Product Issues / Force Majeure / /

Facility

Translational Science University / Translational Science University of Pittsburgh Ivacaftor Overview / /

IndustryTerm

Treatment for Cystic Fibrosis / treatment of cystic fibrosis / /

MedicalCondition

inflammation Progressive lung disease Pancreatic insufficiency / only single-organ dysfunction / Pancreatic Insufficiency Malnutrition CFTR / focal biliary cirrhosis Frequent lung infections / Digestive problems Reduced fertility Infertility / Multi-system Disease Sinus infection / cystic fibrosis transmembrane conductance regulator / Nasal polyps Bile duct obstruction / cystic fibrosis / MS / /

Organization

University of Pittsburgh / Stanford University / Cystic Fibrosis Foundation / Translational Science University / Allergy Drugs Advisory Committee / Advisory Committee / Translational Science University of Pittsburgh Ivacaftor Overview / /

Person

Joseph M. Pilewski / Jeffrey Chodakewitz / Antoinette Paone / Safety Mark Higgins / /

Position

Chief Medical Officer / Professor / Vice President / Senior Clinical Director / Associate Professor / Professor of Medicine / /

Product

thrive / Eight Additional Gating / G551D / ion transport Fluid / R117H / electrolyte imbalance Defective ion transport Lung Disease Infertility / /

ProvinceOrState

South Dakota / /

RadioStation

CFTR / /

SocialTag