Taiwan / Germany / Netherlands / Italy / Northern Ireland / Sweden / New Zealand / Norway / France / Japan / Austria / United States / Australia / United Kingdom / Scotland / South Korea / Greece / Denmark / Wales / /
rare diseases / certain diseases / wake disorder / HAE / hereditary angioedema / neurogenic orthostatic hypotension / cystic fibrosis / very rare diseases / common diseases / less prevalent diseases / serious diseases / lipodystrophy / Haemophilia A / disease / NSCLC / rare disease / Haemophilia B / Gaucher Disease / serious and life-threatening diseases / rare disorders / diseases / only very rare diseases / Multicentric Castleman’s disease / syndrome / disorders / /
MedicalTreatment
chemo / /
Organization
Dept of Health / Therapeutic Goods Administration / Rare Conditions Medicines Fund / European Medicines Agency / South Korea’s Ministry of Food and Drug Safety / US Food and Drug Administration / FDA / European Union / Department of Health / New Medicines Fund / Ministry of Health / /
Person
EMA US FDA / /
Position
Governor / Life Saving Drugs Programme Executive / /
Product
propranolol hydrochloride / OptumRx - Drug / Public Drug / G551D / /