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Wolman disease
Results: 19

#	Item
11	SYNAGEVA BIOPHARMA™ REPORTS POSITIVE TOP-LINE RESULTS FROM PHASE 3 STUDY OF SEBELIPASE ALFA IN CHILDREN AND ADULTS WITH LAL DEFICIENCY Phase 3 Study Meets Primary Endpoint and Six Secondary Endpoints Across Multiple Di Add to Reading List Source URL: www.synageva.com Language: English - Date: 2014-10-09 07:26:12 Medicine Cardiology Lipoproteins Lysosomal Acid Lipase Deficiency Clinical research Cholesteryl ester storage disease Wolman disease Niacin Clinical trial Health Rare diseases Lipid storage disorders
12	SYNAGEVA BIOPHARMA™ ANNOUNCES SATELLITE SYMPOSIUM AT THE NATIONAL LIPID ASSOCIATION MEETING LEXINGTON, Mass., May 2, [removed]Synageva BioPharma Corp. (Synageva) (NASDAQ:GEVA), a biopharmaceutical company developing the Add to Reading List Source URL: www.synageva.com Language: English - Date: 2014-05-02 07:29:47 Wolman disease Cholesteryl ester storage disease Sanfilippo syndrome Mucopolysaccharidosis Lysosomal storage disease Lysosomal Acid Lipase Deficiency Health Rare diseases Lipid storage disorders
13	LAL DEFICIENCY DISEASE REVIEW PUBLISHED IN ATHEROSCLEROSIS LEXINGTON, Mass., April 21, [removed]Synageva BioPharma Corp. (Synageva) (NASDAQ:GEVA), a biopharmaceutical company developing therapeutic products for rare dise Add to Reading List Source URL: www.synageva.com Language: English - Date: 2014-04-21 08:00:38 Medicine Lysosomal Acid Lipase Deficiency Wolman disease Cholesteryl ester storage disease Lysosomal storage disease Acid lipase disease Mucopolysaccharidosis Sanfilippo syndrome Lysosomal lipase Health Rare diseases Lipid storage disorders
14	SYNAGEVA’S SEBELIPASE ALFA RECEIVES BREAKTHROUGH THERAPY DESIGNATION FOR EARLY ONSET LAL DEFICIENCY FROM THE U.S. FOOD AND DRUG ADMINISTRATION LEXINGTON, Mass., May 20, [removed]Synageva BioPharma Corp. (Synageva) (NASD Add to Reading List Source URL: www.synageva.com Language: English - Date: 2013-05-20 07:13:10 Wolman disease Lysosomal Acid Lipase Deficiency Cholesteryl ester storage disease Lysosomal storage disease Mucopolysaccharidosis Sanfilippo syndrome Wolman Acid lipase disease Lysosomal lipase Health Rare diseases Lipid storage disorders
15	SYNAGEVA BIOPHARMA™ HIGHLIGHTS DATA AT THE NASPGHAN MEETING LEXINGTON, Mass., October 11, [removed]Synageva BioPharma Corp. (Synageva) (NASDAQ:GEVA), a biopharmaceutical company developing therapeutic products for rare Add to Reading List Source URL: www.synageva.com Language: English - Date: 2013-10-11 07:24:04 Lipid storage disorders Lysosomal Acid Lipase Deficiency Wolman disease Cholesteryl ester storage disease Sanfilippo syndrome Lysosomal storage disease Hunter syndrome Enzyme replacement therapy Mucopolysaccharidosis Health Medicine Rare diseases
16	SYNAGEVA BIOPHARMA™ HIGHLIGHTS DATA PRESENTATIONS AND SATELLITE SYMPOSIUM AT THE EUROPEAN ATHEROSCLEROSIS SOCIETY CONGRESS LEXINGTON, Mass., June 3, [removed]Synageva BioPharma Corp. (Synageva) (NASDAQ:GEVA), a biopharm Add to Reading List Source URL: www.synageva.com Language: English - Date: 2014-06-03 10:39:51 Medicine Lysosomal Acid Lipase Deficiency Wolman disease Cholesteryl ester storage disease Sanfilippo syndrome Mucopolysaccharidosis Lysosomal storage disease Atherosclerosis Low-density lipoprotein Health Rare diseases Lipid storage disorders
17	Chair Rohit Kohli, MBBS, MS Associate Professor of Pediatrics Medical Director, Complex Surgery and Transplant Inpatient Unit Co-Director, Steatohepatitis Center Add to Reading List Source URL: www.naspghan.org Language: English - Date: 2014-06-18 09:22:16 Hepatology Lipid storage disorders Rare diseases Hepatitis Cholesteryl ester storage disease Non-alcoholic fatty liver disease Cirrhosis Lysosomal Acid Lipase Deficiency Wolman disease Medicine Health Anatomy
18	The people. Their lives. The impact[removed]Annual Report Dear Fellow Shareholders, 2013 was an amazing year for both Synageva and for patients. We met, Add to Reading List Source URL: www.synageva.com Language: English - Date: 2014-04-23 16:54:16 Lipid storage disorders Lysosomal Acid Lipase Deficiency Wolman disease Cholesteryl ester storage disease Orphan drug Hunter syndrome Clinical trial Cirrhosis Sanfilippo syndrome Health Rare diseases Medicine
19	Chair Rohit Kohli, MBBS, MS Associate Professor of Pediatrics Medical Director, Complex Surgery and Transplant Inpatient Unit Co-Director, Steatohepatitis Center Add to Reading List Source URL: www.naspghan.org Language: English - Date: 2014-06-27 11:01:50 Hepatology Lipid storage disorders Rare diseases Hepatitis Cholesteryl ester storage disease Non-alcoholic fatty liver disease Cirrhosis Lysosomal Acid Lipase Deficiency Wolman disease Medicine Health Anatomy