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Medicine / Neurodegenerative disorders / Niemann–Pick disease / Miglustat / Cataplexy / Health / Lipid storage disorders / Rare diseases
Date: 2010-01-14 15:59:00
Medicine
Neurodegenerative disorders
Niemann–Pick disease
Miglustat
Cataplexy
Health
Lipid storage disorders
Rare diseases

|Barb Vorpahl FDA Presentation January 12, 2010 Good Afternoon. My name is Barb Vorpahl, and I am chair of the National Niemann-Pick Disease Foundation. My husband and Gary and I also had a daughter, Stacey who died at t

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