![Medicine / Neurodegenerative disorders / Niemann–Pick disease / Miglustat / Cataplexy / Health / Lipid storage disorders / Rare diseases Medicine / Neurodegenerative disorders / Niemann–Pick disease / Miglustat / Cataplexy / Health / Lipid storage disorders / Rare diseases](https://www.pdfsearch.io/img/a2d5867333a408a1b46035c35f47e024.jpg) Date: 2010-01-14 15:59:00Medicine Neurodegenerative disorders Niemann–Pick disease Miglustat Cataplexy Health Lipid storage disorders Rare diseases | | |Barb Vorpahl FDA Presentation January 12, 2010 Good Afternoon. My name is Barb Vorpahl, and I am chair of the National Niemann-Pick Disease Foundation. My husband and Gary and I also had a daughter, Stacey who died at tAdd to Reading ListSource URL: www.nnpdf.orgDownload Document from Source Website File Size: 53,03 KBShare Document on Facebook
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