| Document Date: 2014-03-04 16:17:18 Open Document File Size: 20,78 KBShare Result on Facebook
Anniversary the 30th anniversary of the Orphan Drug Act and the National Organization / / Company LYN14091 S.L.C. / National LYN14091 S.L.C. / / Country United States / / Event FDA Phase / / IndustryTerm treatment for rare diseases / orphan products / / MedicalCondition pulmonary fibrosis / muscular dystrophy / rare diseases / progeria / diseases / spinal muscular atrophy / epidermolysis bullosa / disorder / sickle cell anemia / cystic fibrosis / childhood cancers / rare disease / rare genetic diseases / disorders / / Organization CONGRESS / SENATE OF THE UNITED STATES / Food and Drug Administration / Senate / National Organization for Rare Disorders / / Position advocate for rare disease research / / Product Patient-Focused Drug / / PublishedMedium Public Law / / Technology Drug Development / /
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