San Francisco / Philadelphia / New York / Washington / DC / Atlanta / Chicago / /
Company
Amgen / Tolerance Working Group / Rare Disease Day US / LAL Solace Liam’s Land Organization Inc. / Facebook / OT Resource / Pfizer Inc. / MitoAction MEBO Research Inc. / Alexion Pharmaceuticals Inc. / Acromegaly Community Inc. / Several Important Bills Were Incorporated / Genentech Inc. / Bray / Parent Project Muscular Dystrophy Short Bowel Syndrome Foundation Inc. / CBS News / Rare Disease Therapeutics Inc. / Wall Street Journal / ABC / NORD / Hemolytic Uremic Syndrome (aHUS) Amgen Inc. / Vertex Pharmaceuticals Inc. / FDA’s / Biogen Idec / Anascorp / Rare Disease Day Partners / FACMG / /
Country
Canada / United States / /
Currency
USD / / /
EntertainmentAwardEvent
Foundation) One One-Year Award / /
Event
M&A / FDA Phase / Natural Disaster / /
Facility
Gene Profiling Facility Samuel Lunenfeld Research Institute Mount Sinai Hospital / FRACP Australian Neuromuscular Research Institute / FDA Center / Mount Sinai Hospital / University Health Network / Pediatric Pathology Loma Linda University / Toronto Western Hospital University of Toronto / University of Toronto Department / White Oak Campus of FDA / PitiéSalpêtrié Hospital / Union Station / Neurobiology University of Southern California Molecular Basis / Washington National Medical Center / Laboratory Medicine / / /
Washington DC Office / Inc. Myotonic Dystrophy Foundation National Brain Tumor Society NBIA Disorders Association NOMID Alliance Parent Project Muscular Dystrophy Short Bowel Syndrome Foundation / Drug Information Association / Tarlov Cyst Disease Foundation / FDA’s office of Orphan Products Development / PitiéSalpêtrié Hospital Paris / Loma Linda University / Senate / NIH Coalition of Patient Advocacy Groups / U.S. Congress / Urea Cycle Disorders Foundation / Laboratory for Advanced Molecular Diagnostics / Food Protein Entercolitis LAL Solace Liam’s Land Organization / Duke University School of Medicine / Center for Devices and Radiological Health / NORD’s RN / office of Special Health Issues / Assistant Professor Broad Center for Regenerative Medicine and Stem Cell Research / Research Project Portfolio Clinical Genomics Center / Genetic Alliance / University of Toronto Department of Laboratory Medicine and Pathobiology Toronto / RDCRN NORD / National Organization for Rare Disorders / Neurobiology University of Southern California Molecular Basis of Split Hand-Foot Malformations / FDA / Corporate Council / Biotechnology Industry Organization / Rare Disease Council / Connecticut Office / NIH FDA / Mount Sinai Hospital / Congressional Childhood Cancer Coalition / Massachusetts Biotechnology Council / National Institute of Health / Shwachman-Diamond Syndrome Foundation / Food and Drug Administration / Expanding and Promoting Expertise in Review of Rare Treatments / Gene Profiling Facility Samuel Lunenfeld Research Institute Mount Sinai Hospital Toronto / FDA Center for Drug Evaluation and Research / Energy & Commerce Committee / FDA’s CDER / Cell and Neurobiology University of Southern California Molecular Basis / Inc. Guthy Jackson Charitable Foundation International Association for Food Protein Entercolitis LAL Solace Liam / Senate HELP Committee / Congress / Inc. MitoAction MEBO Research / Washington National Medical Center / NORD Member Organization / Australian Neuromuscular Research Institute Perth / NIH office of Rare Diseases Research / HELP Committee / Cystic Fibrosis Foundation / NORD’s Medical Advisory Committee / FCCMG Clinical and Metabolic Geneticist Assistant Professor University Health Network/ Mount Sinai Hospital Toronto / Food Safety / House Energy & Commerce Committee / Center for Drug Evaluation and Research / NORD Corporate Council / Department of Cell / University of Toronto / Center for Biologics Evaluation and Research / /
Person
Anne Pariser / Richard Burr / Sheldon Whitehouse / Obama / Gayatri Rao / Mike Enzi / Henry Waxman / Kerby C. Oberg / ABBEY S. MEYERS / Patricia Richardson / Charles Bass / Aaron Goldman / Sarah MacDonald / Paul Kim / John Barrasso / Thomas Marino / Amy Klobuchar / Cliff Stearns / Michael McCaul / Kieran Murphy / Scott Brown / Michael Burgess / Jordan Lerner-Ellis / Blair Van Brunt / Fred Upton / Michael Bennet / Chantal Morel / Robert Casey / Margaret Hamburg / Marshall Summar / Al Franken / Julian Rodrigues / Tom Harkin / Sabine Meunier / Peter L. Saltonstall / Michael Scott / Kay Hagan / Johnny Isakson / Lamar Alexander / Brian Bilbray / Diana DeGette / Steven Grossman / Pamela Gavin / / /
Position
President / Vice President for Communications / founding president / Online Physician / Deputy Chief / Chief / Actress / official / President and CEO / regulatory consultant / Representative / genetic counselor / Associate Professor / Director for Rare Diseases / Principal Investigator / policy leader and advocate / Board Chair / Senator / teacher / President add / Chairman / Hospital Director / International Medical Affairs / Director / Commissioner / Assistant Professor / Professor & Vice Chair / advocate for the rare disease community / patient/researcher / family Neurologist / Senior Researcher Movement Disorders Clinic / Director / International Medical Affairs / NORD President and CEO / /
Product
Rituxan / Sensipar / PAPs / Soliris / Act / /
ProgrammingLanguage
DC / /
ProvinceOrState
New York / Connecticut / Ontario / Maryland / /
PublishedMedium
the ABC and CBS News / Cancer Research / /
Region
Southern California / Western Australia / /
SportsLeague
International Association / /
TVShow
The West Wing / Home Improvement / Strong Medicine / /
Technology
Clinical Genomics / Medical Imaging / Biotechnology / drug development / Regenerative Medicine / /