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Rare diseases / Drug discovery / Orphan drug / Pharmaceuticals policy / Morquio syndrome / Pharmaceutical industry / BioMarin Pharmaceutical / Mucopolysaccharidosis / National Organization for Rare Disorders / Health / Pharmaceutical sciences / Medicine


National Organization for Rare Disorders Remarks before the FDA Endocrinologic and Metabolic Drugs Advisory Committee Silver Spring, Maryland November 19, 2013 Good afternoon. My name is Diane Edquist Dorman, Vice Presid
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Document Date: 2013-11-22 12:36:21


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Company

BioMarin / /

Country

United States / /

IndustryTerm

biopharmaceutical / /

MedicalCondition

Rare disease / rare diseases / rare disorders / Syndrome / /

MedicalTreatment

alternative therapy / /

Organization

FDA / Advisory Committee / National Organization for Rare Disorders Comments / Endocrinologic and Metabolic Drugs Advisory Committee / National Organization for Rare Disorders / National Organization for Rare Disorders Remarks / /

Person

Diane Edquist Dorman / /

Position

Vice President for Public Policy / /

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